Revolutionizing in vivo gene delivery to usher in a new era of genetic medicines.

Mythic Therapeutics

Pioneering a powerful new approach to improving the effectiveness of antibody-drug conjugates (ADCs) and other antibody-based therapeutics.

Ocelot Bio

On a mission to revolutionize treatment options for patients with severe liver disease.

Cyteir Therapeutics

Leader in the discovery and development of novel therapeutics based on the biology of DNA repair and synthetic lethality for the treatment of cancer and autoimmune diseases.


REGENXBIO is the leading next-generation AAV gene therapy company, developing a new class of
personalized therapies based on its proprietary NAVĀ® Technology platform for a range of severe
diseases with serious unmet needs.